Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - Neuromuscular Disorders
Frontiers | Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence
PDF) Characterizing health state utilities associated with Duchenne muscular dystrophy: a systematic review
Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study - Komaki - 2020 - Annals of Clinical and Translational Neurology - Wiley Online Library
Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis | PLOS ONE
PDF) Cost-Effectiveness Analysis of Diagnosis of Duchenne/Becker Muscular Dystrophy in Colombia
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)
CRISPR technologies for the treatment of Duchenne muscular dystrophy: Molecular Therapy
Cost of Illness in Patients with Duchenne Muscular Dystrophy in Portugal: The COIDUCH Study | SpringerLink
PDF) Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls
DMD genotypes and loss of ambulation in the CINRG Duchenne Natural History Study | Neurology
CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies - Chey - WIREs Mechanisms of Disease - Wiley Online Library
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - ScienceDirect
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)
PDF) Genotype characterization and delayed loss of ambulation by glucocorticoids in a large cohort of patients with Duchenne muscular dystrophy
Genes | Free Full-Text | Current Outline of Exon Skipping Trials in Duchenne Muscular Dystrophy | HTML
New variants, challenges and pitfalls in DMD genotyping: implications in diagnosis, prognosis and therapy | Journal of Human Genetics
Nutrients | Free Full-Text | Metabogenic and Nutriceutical Approaches to Address Energy Dysregulation and Skeletal Muscle Wasting in Duchenne Muscular Dystrophy | HTML
Muscle membrane integrity in Duchenne muscular dystrophy: recent advances in copolymer-based muscle membrane stabilizers | Skeletal Muscle | Full Text
Vicious cycle of postural instability that leads to loss of ambulation... | Download Scientific Diagram
A new era in the management of Duchenne muscular dystrophy - Korinthenberg - 2019 - Developmental Medicine & Child Neurology - Wiley Online Library
Structure-activity relationships of 2-pyrimidinecarbohydrazides as utrophin modulators for the potential treatment of Duchenne muscular dystrophy - ScienceDirect
